RARE DISEASE DAY 2022

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RDD 2022 - Rare But Not Alone

ROCKET PHARMA CELEBRATES RARE DISEASE DAY 2022

Rare, but Not Alone

Our mission is to seek gene therapy cures for people living with rare diseases, who are our North Star. During Rocket’s Rare Disease Day 2022 celebration, 250+ members of the rare disease community and Rocket team gathered at the NASDAQ Tower in Times Square and virtually.

Introduction to Rare Disease Day

Kinnari Patel, PharmD, MBA

Danon Disease & Multi-Generational Care: A Rare Patient and Family Story

Moderator: Latika Hickey, PharmD

Speaker Panel: Dawn, Barbara, Steven, and Gabriel

Rare Innovations: Harnessing Collaboration to Drive Medical Innovation in DanonDisease

Moderator: Gaurav Shah, MD

Keynote Speaker: MorisDanon, MD

Speaker Panel: Matthew Taylor, MD, PhD; Eric Adler, MD; Barry Greenberg, MD; Joseph Rossano, MD

Rare Resources

RTW Foundation: Deborah Slipetz, PhD

DanonFoundation: Kim Marincik, Jenny Hsieh, Amy Atkinson

National Organization for Rare Disorders (NORD): Debbie Drell

Rare, But Not Alone

Mousumi Bose, PhD

Danielle Kinsey, MD

Lucas and Emma (PKD)

Paul and Barbara (IMO)

Shaping Foundations

About Shaping Foundations

“I Support Rare”

Closing Remarks & Musical Performance

Gaurav Shah, Falu, Sarosh Effendi

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