DNA Is No Longer Destiny
Seeking gene therapy cures that correct rare and devastating diseases at their root cause. Cures that represent freedom – freedom for patients and their loved ones to fully live in a world without the burden of genetic disease. A world where DNA is not destiny and genetic disease is history.
Mission, Vision & Values
Our mission is to seek gene therapy cures for patients with devastating rare diseases through the most innovative science and platforms to fulfill the promise of gene therapy for the betterment of our industry, science and humanity.
Trust
Generosity
Curiosity
Elevate
Patient Community
Patients and their caregivers are our North Star—the inspiration and guiding force behind everything we do. We are also acutely aware that rare diseases have a ripple effect, impacting the lives of patients as well as the families, friends, and caregivers who love them. We aim to create a community where rare disease patients and their families can come together and feel supported through every step of their journey.
Our Science
Our thoughtful multi-platform approach gives our team the unique advantage to develop therapies specifically for conditions with high unmet needs. This allows us to seek diseases where cures seem impossible or those that are often overlooked. Having the flexibility to select the best platform for the disease—ex vivo lentiviral (LV) or in vivo adeno-associated viral (AAV) — keeps patients at the core of everything we do.
Our People
The Rocket team possesses decades of experience and leadership in the biotech industry. This expertise, combined with our passion, creativity, a commitment to patients and curiosity, has enabled us to build and advance a pipeline of programs targeting genetic bone marrow-derived and cardiovascular diseases.
