Clinical Trials

Clinical Trials - Girl Painting with Hand

Rocket is committed to the development of first-in-class and best-in-class gene therapies for the treatment of rare, genetic disease. Each of Rocket’s five gene therapy programs is currently being evaluated in a clinical trial.

Patients and families interested in accessing educational and advocacy group resources about any of these indications addressing should visit our Patients and Community page to learn more.

If you are a patient or family member and are interested in potentially enrolling in one of our trials, please contact us.

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