AAV Presentations and Posters 2023 Presentations Danon Disease: RP A501 Phase 1 Results The First Single Dose Intravenous (IV) Gene Therapy with Recombinant Adeno Associated Virus (AAV9:LAMP2B) for a Monogenic Cardiomyopathy (Click to download)Preclinical Efficacy of AAVrh.74 PKP2a (RP A601): Gene Therapy for PKP2 associated Arrhythmogenic Cardiomyopathy (PKP2 ACM) (Click to download) 2022 Presentations HFSA: Danon Disease Phase 1 Update (Click to download)ASGCT: Danon Disease Phase 1 Update (Click to download) 2021 Presentations Danon 2021 Phase 1 Update (Click to download) 2020 Presentations Danon Data (Click to download)