ASGCT Presentations & Posters 2022 Presentations Danon 2022 Phase 1 Update (Click to download)Gene Therapy for Fanconi Anemia (Group A): Interim Results of RP-L102 Clinical Trials (click to download)Changing the Treatment Paradigm for Pyruvate Kinase Deficiency with Lentiviral Mediated Gene Therapy: Interim Results from an Ongoing Global Phase 1 Study (click to download)POSTER: Changing the Treatment Paradigm for Pyruvate Kinase Deficiency with Lentiviral Mediated Gene Therapy: Interim Results from an Ongoing Global Phase 1 Study (click to download)Interim Results From an Ongoing Phase 1/2 Study of LentiviralMediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I) (click to download)
