ASGCT Presentations & Posters
A Phase 1/2 Study of Lentiviral-mediated Ex vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency I (LAD I): Initial Results from the First Treated Patient (click to download)
Updated Results of a European Gene Therapy Trial in Fanconi Anemia Patients, Subtype A (click to download)
Poster: Lentiviral Vector-mediated Gene Complementation for the Diagnosis of LAD-I (click to download)